Study of EN-374 Gene Therapy in Participants With X-Linked Chronic Granulomatous Disease

Abstract

The goal of this clinical trial is to evaluate the safety and potential efficacy of the EN-374 treatment regimen and identify a dose level for further evaluation in participants with x-linked chronic granulomatous disease. The main questions it aims to answer are: * safety of the EN-374 treatment regimen * effect of the EN-374 treatment regimen on the production of functional neutrophils with NADPH oxidase activity Phase: PHASE1, PHASE2 Status: RECRUITING Conditions: X-Linked Chronic Granulomatous Disease Interventions: EN-374

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